CRISPR-Tech @CRISPR-Tech: "First Crispr Therapy Gets FDA..."

United Kingdom

First Crispr Therapy Gets FDA Nod for Sickle Cell Disease 👉 The US Food and Drug Administration approved the first gene editing therapy using CRISPR technology on Friday, a collaboration between $VRTX (Vertex Pharmaceuticals Incorporated) and $CRSP (CRISPR Therapeutics AG) for treating sickle cell disease. 👉 Called Casgevy, the approval will allow the drug to come to market in the US. Sickle cell disease affects some 100,000 Americans. Vertex says Casgevy is meant for the around 20,000 that have a severe version of the illness. The disease can land some people in the hospital multiple times a year. 👉 The treatment works by precisely targeting changes in DNA to repair flaws in patients’ genomes related to the inherited disease. It promises a potential cure but requires undergoing an intense several-month treatment process and costs $2.2 million. It’s unclear whether insurers will widely cover the therapy or if many sickle cell patients will take it. 👉 The FDA’s approval is a positive sign for the burgeoning field of gene editing, which makes permanent changes in human DNA in order to treat — and potentially cure — diseases. Drug companies and patients are looking to gene-editing technology to fix some of the most intractable disorders, such as sickle cell disease. The FDA’s blessing is a sign that regulators believe the benefits of the one-time treatment outweigh any potential safety concerns about altering human DNA. Read more ❓ www.bloomberg.com/news/articles/2023-12-08/first-crispr-treatment-for-sickle-cell-approved-by-us-regulators $VRTX and $CRSP are part of eToro’s @CRISPR-Tech Smart Portfolio. This portfolio is composed of stocks of leading companies in the gene-editing field of research and development. This industry could have critical applications in various walks of life, such as farming and biotechnology, among others. Your capital is at risk. Past performance is not an indication of future results.

5 Mentioned

VRTX

Vertex Pharmaceuticals Incorporated

CRSP

CRISPR Therapeutics AG

VRTX

Vertex Pharmaceuticals Incorporated

CRSP

CRISPR Therapeutics AG

CRISPR-Tech